Highly efficient neuronal gene knockout in vivo by CRISPR-Cas9 via neonatal intracerebroventricular injection of AAV in mice

Sam Hana, Michael Peterson, Helen McLaughlin, Eric Marshall, Attila J. Fabian, Olivia McKissick, Kathryn Koszka, Galina Marsh, Michael Craft, Shanqin Xu, Alexander Sorets, Tess Torregrosa, Chao Sun, Chris E. Henderson, Shih-Ching Lo

Gene Ther (2021). https://doi.org/10.1038/s41434-021-00224-2